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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Cachexia
DHPR α1S
Inbred C57BL
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Knockout
Muscles/physiopathology
LncRNA
Delivery
Duchenne muscular dystrophy DMD
Animal/physiopathology
Humans
L-Type
DMD
MiARN
Inbred mdx
Gene modifiers
Molecular Sequence Data
Base Sequence
NNOS
Dystrophin
Liver
Calcium
Gene Expression Regulation/drug effects
Metabolism
MES
Cell homeostasis
Energy Metabolism/drug effects
Dystrophin-EGFP
Autophagy
Mice
Dystrophie Musculaire de Becker BMD
Becker muscular dystrophy BMD
Mdx mouse
Cultured
Becker muscular dystrophy
CaV subunits
Diseases
Long noncoding RNA
Clinical trials
Génomique
Calcium Channels
Dynamin 2
Immunoglobulin Fc Fragments/pharmacology
Hear
Cells
Duchenne muscular dystrophy
Ex-vivo
NAD+
Dystrophie musculaire de Becker
Homeostasis
Activin Receptors
Centronuclear myopathy
LncARN
CaVβs
Long QT
Becker BMD muscular dystrophy
Muscular dystrophy
Duchenne DMD dystrophy
Molecular docking
Multi exon skipping
Hepatocellular carcinoma
Cardiomyopathy
Exon skipping
Male
Cell Line
Human Umbilical Vein Endothelial Cells
Muscle Biology
Muscular Dystrophy
CD38
Multi resolution modeling
Gene expression
Cardiomyopathie
Antisense oligonucleotides
Skeletal muscle
Dystrophy
Muscle Strength
BMD
Modificateurs de gènes
Dystrophie Musculaire de Duchenne DMD
Multiresolution modeling
Genomic
Muscle development
Muscle
Morphogenesis
DMO
CTNNB1
Muscular Atrophy
Myogenesis
Cell Biology
LKB1
Dystrophin central domain
Animals
Dystrophine
Allele‐specific silencing therapy
Drp1
Epigenetics
Inhibitors
Myotendinous junction
Mitochondrial fission
Invivo