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Myoblasts
CMS
Therapy
Myotonic dystrophy type 1
Laminopathie
Duchenne muscular dystrophy
Rare neuromuscular diseases
Trinucleotide repeat expansion
Congenital muscular dystrophy
Male
LMNA
Autoimmunity
Biomarker
Satellite cells
Alternative splicing
Regeneration
Treatment
Antisense oligonucleotides
Neuromuscular disease
Thérapie génique
Actin
OPMD
Aged
Cell therapy
Myotonic dystrophy
Fabry disease
Humans
LMNA gene
Myopathies
Transcriptomics
Calcium
Laminopathies
Cardiomyopathy
CTG repeat contractions
Diagnosis
Cytoskeleton
Amyotrophic lateral sclerosis
Myasthenia Gravis MG
Cancer
Thymus
Astrocyte
Satellite cell
Outcome measures
Congenital myopathy
CRISPRi
Cytokines
Myasthenia gravis
Brain
RNA interference
RNA biology
Motoneuron
Neuromuscular diseases
PABPN1
AAV
Glutamate
Muscle
Centronuclear myopathy
Genotype phenotype correlation
DMD
Gene therapy
Myotonic Dystrophy type 1
Neuromuscular junction
COVID-19
Nuclear envelope
Clinical trials
Lamin A/C
Dermatomyositis
Mouse model
Muscle regeneration
Errance diagnostique
Myogenesis
Lamin A/C LMNA gene
ALS
Autoimmune diseases
Muscular dystrophy
FSHD
Myositis
Laminopathy
Animals
Exercise
Heart
Skeletal muscle
Autoantibodies
Heart failure
Dystrophin
Dilated cardiomyopathy
Transgenic mouse model
Dynamin 2
MBNL
Autophagy
Myotonic Dystrophy
Fibrosis
Inflammation
Becker muscular dystrophy
Myopathy
Rare diseases
Mechanotransduction
Aging
Long read sequencing
Biomarkers